On Rare Disease Day we want to take a moment to thank all scientists, physicians and patients who work together in the Charlie project to develop and validate new therapies and biomarkers to avoid brain damage in GA1 and PDE.

Progress is presented and discussed in frequent online meetings and a face 2 face meeting will take place with the Charlie Consortium in Munich on April 29 and 30, 2024. The German Mouse Clinic will be hosting this event.

For more information on Rare Disease Day please visit the website: https://www.rarediseaseday.org/